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Table 2 Distribution of RPD designations per disease

From: Analysis of the first ten years of FDA’s rare pediatric disease priority review voucher program: designations, diseases, and drug development

Disease breakdown

Number of diseases

Percentage of total diseases (n = 245) (%)

Percentage of total RPD designations (n = 569) (%)

Number of diseases associated with 1 RPD designation

152

62

27

Number of diseases associated with 2 RPD designations

32

13

11

Number of diseases associated with 3 RPD designations

18

7

9

Number of diseases associated with 4 RPD designations

17

7

12

Number of diseases associated with 5 or more RPD designations

26

11

41

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Orphanet Journal of Rare Diseases

ISSN: 1750-1172