Skip to main content

Table 1 RPD designations by therapeutic areas, 2013–2022

From: Analysis of the first ten years of FDA’s rare pediatric disease priority review voucher program: designations, diseases, and drug development

Therapeutic area

Number of RPD designations

Percentage of total RPD designations (%)

Number of diseases associated with at least 1 RPD designation within therapeutic area

Number of RPD designations per disease within therapeutic area

Neurology

149

26

63

2.4

Metabolism

131

23

70

1.9

Oncology

105

18

22

4.8

Hematology

32

6

8

4

Immunology

25

4

16

1.6

Ophthalmology

22

4

16

1.4

Dermatology

21

4

10

2.1

Pulmonary

15

3

6

2.5

Orthopedics

15

3

6

2.5

Endocrinology

12

2

6

2

Gastroenterology

12

2

7

1.7

Cardiology

9

2

5

1.8

Infectious diseases

9

2

6

1.5

Otorhinolaryngology

5

1

2

2.5

Nephrology/urology

4

1

3

1.3

Transplant

2

< 1

2

1

Pharmacology/toxicology/poisoning/chelators

1

< 1

1

1

Back to article page

Orphanet Journal of Rare Diseases

ISSN: 1750-1172