# | Sex | Prior therapy | Genotype | Phenotype | Weight(Kg) | Anti-drug antibodies (titer)a | |||||||
---|---|---|---|---|---|---|---|---|---|---|---|---|---|
Baseline | 1st mo | 2nd mo | 3rd mo | 4th mo | 5th mo | 6st mo | 12th mo | ||||||
1 | M | naïve | p.I354K | Classic | 69 | 0 | |||||||
2 | M | naïve | p.P265L | Classic | 74 | 0 | |||||||
3 | F | alfa | p.A156V | Classic | 48 | 0 | |||||||
4 | M | naïve | c.1213 delA | Classic | 60 | 0 | POS3200 | POS6400 | |||||
5 | F | naïve | c.1213 delA | Classic | 56 | 0 | IARs | ||||||
6 | M | naïve | c.1213 delA | Classic | 45 | 0 | POS3200 | POS800 | POS800 | ||||
7 | F | naïve | c.1213 delA | Classic | 58 | 0 | |||||||
8 | F | naïve | c.1213 delA | Classic | 67 | 0 | |||||||
9 | F | naïve | p.L414Cfs*3 | Classic | 58 | 0 | |||||||
10 | M | alfa | p.N215S | Late-onset | 83 | 0 | POS3200 | POS1600 | NEG | NEG | NEG | ||
11 | F | naïve | p.S235C | Classic | 64 | 0 | |||||||
12 | F | naïve | c.583insG | Classic | 55 | 0 | |||||||
13 | M | naïve | c.388 A > G | Classic | 70 | 0 | |||||||
14 | M | naïve | c.1284_1287delA | Classic | 73 | 0 | |||||||
15 | F | alfa | p.L275H | Classic | 48 | 0 | |||||||
16 | F | naïve | p.F113L | Late-onset | 67 | 0 | |||||||
17 | F | naïve | p.F113L | Late-onset | 66 | 0 | |||||||
18 | M | naïve | p.F113L | Late-onset | 65 | 0 | |||||||
19 | F | naïve | p.F113L | Late-onset | 52 | 0 | |||||||
20 | F | naïve | p.F113L | Late-onset | 64 | 0 | |||||||
21 | M | alfa | p.F273S | Classic | 65 | 0 | |||||||
21 | F | alfa | p.R301P | Classic | 51 | 0 | |||||||
23 | F | alfa | p.G260E | Classic | 79 | 0 | POS200 | NEG | |||||
24 | M | naïve | c.1234 A > C | Classic | 57 | 0 | |||||||
25 | M | naïve | IVS5 + 1G > T | Classic | 59 | 0 | POS6400 | POS3200 | POS1600 | POS1600 | NEG | ||
26 | M | naïve | c.1234 A > C | Classic | 60 | 0 | |||||||
27 | M | naïve | c.1234 A > C | Classic | 60 | 0 | |||||||
28 | F | naïve | c.1234 A > C | Classic | 59 | 0 | |||||||
29 | M | naïve | p.I303F | Late-onset | 83 | 0 | POS800 | POS800 | |||||
30 | F | naïve | p.G85D | Classic | 55 | 0 | |||||||
31 | M | naïve | p.N215S | Late-onset | 92 | 0 |