Fig. 1

Overview of recommended therapy strategies for patients with AADC deficiency following treatment with gene therapy. Recommended therapy strategies and their primary intended goal for patients with AADC deficiency following treatment with gene therapy are displayed. The treatment team should work in collaboration with the patient/caregiver to develop a treatment plan that is most appropriate for each patient as they progress following gene therapy. SBI sensory-based interventions, SIT sensory integration therapy