| Request for nusinersen (n = 46) | Request for risdiplam (n = 54) | P value |
---|---|---|---|
Age at inclusion | 39.45 | 32.63 | 0.002 |
Men | 25 | 22 | 0.272 |
MFM32 (n) | 65.54 (n = 13) | 24.80 (n = 10) | 0.002 |
Type 2: n (%) | 3 (7.1%) | 30 (65.2%) | 0.000001 |
Type 3: n (%) | 37 (88.1%) | 15 (32.6%) | 0.00001 |
Walking with aid (%) | 12 (28.6% =  | 3 (6.5%) | 0.06 |
Wheel-chair bound (%) | 23 (54.8%) | 39 (84.8%) | 0.012 |
Eating alone (%) | 29 (85.3%) | 15 (38.5%) | 0.00001 |
Eating with help (%) | 4 (11.8%) | 12 (30.8%) | 0.00001 |
Depending on food (%) | 0 (0.0%) | 8 (20.5%) | 0.0001 |
Feeding tube (%) | 1 (2.9%) | 4 (1.3%) | 0.00001 |
Spine fusion surgery (%) | 10 (25.0%) | 35 (81.4%) | 0.0001 |
No ventilation (%) | 35 (85.4%) | 16 (36.4%) | 0.0001 |
Non invasive ventilation (%) | 6 (14.6%) | 18 (40.9%) | 0.0001 |
Invasive ventilation (%) | 0 (0.0%) | 10 (22.7%) | 0.0001 |