Table 1 Median and range of the baseline score of patients in the natural history cohort
Domains | Natural history scores at baseline (median, range) |
|---|---|
Expressive language (VABS-II) | Median 63, range 22–162 |
Daily living skills (VABS-II) | Median 30.5, range 28–47 |
Gross-motor (VABS-II) | Median 58, range 0–74 |
Sleep (CSHQ) | Median 4, range 0–10 |
Pain (ITQOL) | Median 75, range 25–100 |