Therapeutic goal | N = 20 |
---|---|
Number of therapeutic goals achieved | Â |
 ≤ 1 | 0 (0) |
 2 | 1 (5.0) |
 3 | 0 (0) |
 4 | 3 (15.0) |
 5 | 2 (10.0) |
 6 | 14 (70.0) |
Hepatomegaly score, achieved (score = 0) | 17 (85.0) |
 0 | 17 (85.0) |
 1 | 3 (15.0) |
 2 | 0 (0) |
 3 | 0 (0) |
Splenomegaly score, achieved (score = 0) | 18 (90.0) |
 0 | 18 (90.0) |
 1 | 1 (15.0) |
 2 | 0 (0) |
 3 | 1 (5.0) |
Anemia, hemoglobin count (g/dL), n | 20 |
 Achieveda | 17 (85.0) |
 Mean (SD) | 12.7 (1.9) |
 Median (min–max) | 12.5 (7.8–15.9) |
Thrombocytopenia, platelet count (× 103/μL), n | 20 |
 Achievedb | 18 (90.0) |
 Mean (SD) | 248.2 (102.4) |
 Median (min–max) | 233.0 (24.0–473.0) |
Bone pain, achieved (absent or very mild, or mild) | 18 (90.0) |
 Absent or very mild pain | 17 (85.0) |
 Mild pain | 1 (5.0) |
 Moderate pain | 2 (10.0) |
 Severe pain | 0 (0) |
 Intolerable pain | 0 (0) |
Bone crisis, achieved (absent) | 20 (100) |
 Absent | 20 (100) |
 Present | 0 (0) |