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Fig. 1 | Orphanet Journal of Rare Diseases

Fig. 1

From: Natural history comparison study to assess the efficacy of elamipretide in patients with Barth syndrome

Fig. 1

Study Design for TAZPOWER. AEs = Adverse Events; BTHS-SA = BarTH Syndrome Symptom Assessment; CGIS = Clinician Global Impression of Symptom Severity and Change Scale; 5XSST = Five Times Sit-to-Stand Test; HHD = Hand Held Dynamometry; PGI-S = Patient Global Impression of Symptom Severity and Change Scale; PROMIS F-SF = Patient-Reported Outcomes Measurement Information System Fatigue-Short Form; 6MWT = 6-Minute Walk Test; SWAY = SWAY Application Balance Assessment

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Orphanet Journal of Rare Diseases

ISSN: 1750-1172