Patient 10a | Patient 11a | Patient 12a | Patient 13a | Mean (SD) | |
---|---|---|---|---|---|
PedsQL total score at baseline | 23.9 | 85.9 | 84.8 | 58.7 | 63.3 (29.1) |
Change in PedsQL total score at Week 52 | 21.7 | − 14.1 | 9.8 | – | 5.8 (18.3) |
Percent change in PedsQL total score at Week 52 | 90.9 | − 16.5 | 11.5 | 28.7 (55.7) P = 0.0106 | |
PF | 21.9 | − 18.8 | 15.6 | – | 6.3 (21.9) |
PH | 21.7 | − 11.7 | 6.7 | – | 5.6 (16.7) |
Body weight, percent change | − 26.2 | − 30.2 | − 35.6 | − 27.3 | − 29.8 (4.2) |
Most hunger, percent change | − 54.7 | − 37.5 | − 1.4 | − 3.5 | − 24.3 (26.2) |