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Table 2 Payer coverage criteria for onasemnogene abeparvovec for spinal muscular atrophy

From: Patients’ access to rare neuromuscular disease therapies varies across US private insurers

 

Plan imposes additional coverage criteria

Covered types of SMA

Required number of copies of SMN2 gene

Age requirement

Coverage for advanced SMA*

Prescriber requirement

Plan 1

Yes

NA

NA

 < 2 years

No

Neurologist with expertise in SMA

Plan 2

Yes

1 only

1 or 2 copies

 < 2 years

NA

NA

Plan 3

Yes

NA

1, 2, or 3 copies

 < 2 years

No

Neurologist

Plan 4

Yes

NA

1, 2, or 3 copies

 < 2 years

No

Neurologist with expertise in SMA

Plan 5

Yes

NA

1, 2, or 3 copies

 < 2 years

No

Neurologist with expertise in SMA

Plan 6

Yes

NA

1, 2, or 3 copies

 < 2 years

No

Neurologist with expertise in SMA

Plan 7

Yes

1 only

1, 2, or 3 copies

 < 2 years

No

Neurologist with expertise in SMA

Plan 8

Yes

NA

1, 2, or 3 copies

 < 2 years

No

NA

Plan 9

Yes

1 only

2 copies

 < 9 months

No

Neurologist with expertise in SMA

Plan 10

Yes

1 only

1, 2, or 3 copies

 < 2 years

No

Neurologist

Plan 11

Yes

NA

1, 2, or 3 copies

 < 2 years

No

Neurologist with expertise in SMA

Plan 12

Yes

1 or 2

1, 2, or 3 copies

 < 2 years

No

Neurologist with expertise in SMA

Plan 13

No policy

No policy

No policy

No policy

No policy

No policy

Plan 14

Yes

NA

2 or 3 copies

 < 2 years

NA

NA

Plan 15

Yes

NA

1, 2, or 3 copies

 < 2 years

No

Neurologist

Plan 16

Yes

NA

1 or 2 copies

 < 2 years

No

Neurologist with expertise in SMA

Plan 17

Yes

1 or 2

1, 2, or 3 copies

 < 2 years

No

Neurologist with expertise in SMA

  1. NA = Payer did not address criterion in their coverage policy; *Insurers typically define advanced SMA as patients with complete paralysis of limbs, or on permanent ventilator dependence
  2. NA not available, SMA spinal muscular atrophy, SMN survival motor neuron