Fig. 4From: Sebelipase alfa enzyme replacement therapy in Wolman disease: a nationwide cohort with up to ten years of follow-upAll the Wolman disease (WD) patients treated with sebelipase alfa survived in our cohort. Proportion of survival in WD patients treated with enzyme replacement therapy (ERT, n = 5) compared with WD patients from a historical cohort (LAL-1-NH01 [16], n = 21)Back to article page