Table 3 Burden of disease in a population of adult patients with MPS IVA in Spain
Variable | Value, n (%) (N = 33) |
|---|---|
Mobility problems | 26 (78) |
Mild | 9 (27.3) |
Moderate | 3 (9) |
Severe | 14 (42.2) |
Wheelchair use | 22 (66.7) |
Always | 12 (36.4) |
Need help with self-care | 29 (87.9) |
Fully dependent | 11 (33.3) |
Need help with daily activities | 25 (75.7) |
Mild help | 6 (18.2) |
Moderate help | 8 (24.2) |
Fully dependent | 11 (33.3) |
Pain | 26 (78.8) |
Mild | 13 (39.4) |
Moderate | 9 (27.3) |
Severe | 4 (12.1) |
Anxiety/depression | 8 (24.2) |