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Table 1 Characteristics of enrolled patients with Gaucher disease

From: Economic burden and health related quality of life of ultra-rare Gaucher disease in China

Items

Sample (n)

Proportion (%)

Sex

  

 Male

25

51.0

 Female

24

49.0

Age group (mean age at survey) in years

  

 0–4

19

38.9

 5–7

5

10.2

 8–12

12

24.5

 13–14

2

4.1

 ≥ 15

11

22.5

Age at onset, years

  

 Mean ± SD

9.3 ± 10.69

 

 Max

44

 

 Min

1

 

Disease course from symptom onset, days

  

 Mean ± SD

3.5 ± 3.1

 

 Max

12.1

 

 Min

0.3

 

 Median

2.0

 

Types of Gaucher disease (GD)

  

 Type I

20

40.8

 Type II

5

10.2

 Type III

4

8.2

 Not clear

20

40.8

Number of caregivers

  

 1

28

57.1

 ≥ 2

21

42.9

  1. SD standard deviation