From: Validation of the 5-domain Niemann-Pick type C Clinical Severity Scale
Visit | Collapsed / Uncollapsed | Anchor Category | N | Mean Change (SD) | 95% CI | Effect Size | Median Change |
---|---|---|---|---|---|---|---|
Visit 1 to 6 | Collapsed | No Change | 18 | 0.83 (2.176) | (-0.249, 1.915) | 0.38 | 0.00 |
Worsening | 13 | 2.69 (3.225) | (0.744, 4.641) | 0.83 | 2.00 |