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Table 1 Summary demographic/ambulation data

From: 10th European Conference on Rare Diseases & Orphan Products (ECRD 2020)

 NP-CDMD
Demographicsn = 10n = 8
Age (median) in years1011
Age (range) in years6–149–15
Sex M:F6:48:0
6MWT (m)n = 8n = 8
Mean (SD)444 (± 201.7)322.4 (± 120.5)
Median450325
Range109–772178–522
Mean values for wearable metrics at baselinen = 4n = 6
Average daily maximum1450.82848.28
Average daily steps9582.714504.66
Average daily steps per 30 min epoch392.37214