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Table 1 Summary demographic/ambulation data

From: 10th European Conference on Rare Diseases & Orphan Products (ECRD 2020)

 

NP-C

DMD

Demographics

n = 10

n = 8

Age (median) in years

10

11

Age (range) in years

6–14

9–15

Sex M:F

6:4

8:0

6MWT (m)

n = 8

n = 8

Mean (SD)

444 (± 201.7)

322.4 (± 120.5)

Median

450

325

Range

109–772

178–522

Mean values for wearable metrics at baseline

n = 4

n = 6

Average daily maximum

1450.82

848.28

Average daily steps

9582.71

4504.66

Average daily steps per 30 min epoch

392.37

214