From: 10th European Conference on Rare Diseases & Orphan Products (ECRD 2020)
 | NP-C | DMD |
---|---|---|
Demographics | n = 10 | n = 8 |
Age (median) in years | 10 | 11 |
Age (range) in years | 6–14 | 9–15 |
Sex M:F | 6:4 | 8:0 |
6MWT (m) | n = 8 | n = 8 |
Mean (SD) | 444 (± 201.7) | 322.4 (± 120.5) |
Median | 450 | 325 |
Range | 109–772 | 178–522 |
Mean values for wearable metrics at baseline | n = 4 | n = 6 |
Average daily maximum | 1450.82 | 848.28 |
Average daily steps | 9582.71 | 4504.66 |
Average daily steps per 30 min epoch | 392.37 | 214 |