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Table 7 PROMs: concepts measured in each category

From: To what degree are orphan drugs patient-centered? A review of the current state of clinical research in rare diseases

MEASURED QUANTITY: PROM frequencyHRQOLSymptomsPsychological and cognitive functioningPhysical functioningOther
Generic943612
Non-rare disease specific10111052
Rare disease specific167247
Study-specific19005
Total3631151516