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Table 6 PROMs: categories used in each context of use

From: To what degree are orphan drugs patient-centered? A review of the current state of clinical research in rare diseases

Measured quantity: PROM frequencyNumber of articles publishedGenericNon-rare diseaseRare disease specificStudy-specificTotal PROMs
Observational study/registry4919269761
Clinical trials40121310742
Questionnaire development/validation207318230