Skip to main content

Table 5 PROM mentions: Concepts measured in each context of use

From: To what degree are orphan drugs patient-centered? A review of the current state of clinical research in rare diseases

Measured quantity: Mention frequencyNumber of articles publishedHRQoLSymptomsPsychological and cognitive functioningPhysical functioningOtherTotal
Observational study/registry4934151381787
Clinical trial401926241566
Questionnaire development/validation2096151132