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Fig. 1 | Orphanet Journal of Rare Diseases

Fig. 1

From: Bringing everyone to the table – findings from the 2018 Phelan-McDermid Syndrome Foundation International Conference

Fig. 1

Clinical Trials Update table discussion topics of concern. Demonstrates the top five concerns raised by families during the clinical trials session. Families of both young children and adult patients expressed concerns that clinical trials included narrow age ranges, while all age groups expressed concerns regarding the travel and financial burden to families who participate in research studies

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Orphanet Journal of Rare Diseases

ISSN: 1750-1172