Table 5 Guidance statement for HSCT
From: Recommendations for the management of MPS IVA: systematic evidence- and consensus-based guidance
Statement | Percentage consensus |
|---|---|
Due to the lack of evidence, HSCT cannot be recommended for patients with MPS IVA and at this time is considered an investigational procedure Evidence Grade: D (level 3/4 studies with inconsistent risk/benefit results) | 91% |