Skip to main content

Table 6 Summary of MAD scores (in clinical severity units) comparing predicted and actual disease progression based on first or mean ASIS scores for seizure and non-seizure groups

From: Annual severity increment score as a tool for stratifying patients with Niemann-Pick disease type C and for recruitment to clinical trials

Patient Group First ASIS (severity score units) Mean ASIS (severity score units)
No seizures 1.73 1.28
At least one seizure 6.77 4.26
\