From: Characteristics of drugs for ultra-rare diseases versus drugs for other rare diseases in HTA submissions made to the CADTH CDR
Reason
DURDs N = 9
DORDs N = 13
Clinical only, n (%)
8 (88.9)
8 (61.5)
Cost only, n (%)
1 (11.1)
1 (7.7)
Clinical and cost, n (%)
0 (0)
4 (30.8)