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Table 3 Reasons for negative reimbursement recommendations for DURDs and DORDs

From: Characteristics of drugs for ultra-rare diseases versus drugs for other rare diseases in HTA submissions made to the CADTH CDR

Reason

DURDs N = 9

DORDs N = 13

Clinical only, n (%)

8 (88.9)

8 (61.5)

Cost only, n (%)

1 (11.1)

1 (7.7)

Clinical and cost, n (%)

0 (0)

4 (30.8)