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Table 1 Definitions of terminology used in the current study

From: Characteristics of drugs for ultra-rare diseases versus drugs for other rare diseases in HTA submissions made to the CADTH CDR

Term Definition
Drugs for rare diseases (DRDs) Drugs used to treat diseases that affect ≤ 50 per 100,000 people.
Drugs for ultra-rare diseases (DURDs) Drugs used to treat diseases that affect ≤ 1 per 100,000 people. -
Drugs for other rare diseases (DORDs) Drugs used to treat rare diseases that affect > 1 to 50 per 100,000 people.