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Table 4 Availability of brand name and generic orphan drugs surveyed in 24 public tertiary hospitals in China

From: The availability and affordability of orphan drugs for rare diseases in China

Availability

Range

Originator Brands (Brand Name)

Generics

Absent

0

Ambrisentan (Volibris), Somatropin (Genotropin), Dasatinib (Sprycel), Meisoindigo

None

Very low

<30 %

Imiglucerase (Cerezyme), Sapropterin dihydrochloride (Kuvan), Coagulation factor VIIa (Novoseven), Bosentan (Tracleer), Iloprost (Ventavis), Somatropin (Saizen), Somatropin (Humatrope), Busulfan(Busulfex), Imatinib Mesylate Cap (Glivec), Nilotinib (Tasigna), Riluzole ( Rilutek)

Teniposide, Riluzole taba, Riluzole capa

Low

30–49 %

Recombinant coagulation factor VIII (Kogenate FS), Imatinib mesylate Tab (Glivec), Arsenious acid(Yitaida), Sorafenib (Nexavar)

Human coagulation factor VIII, Danazol

Fairly high

50–80 %

Teniposide (Vumon), Rituximab (MabThera), Poractant alfa (Curosurf)

Human prothrombin complex concentrate,

Recombinant human growth hormone, Mitoxantrone, Homoharringtonine

High

80 %

None

None

  1. a:Tab: Tablets, Cap: Capsules