Study type
|
Case report
|
Cohort prospective
|
---|
Studies
|
Franz 2006
|
Wienecke 2006
|
Birca 2010
|
Lam 2010
|
Krueger 2010
|
Dabora 2011
|
Lopez 2011
|
Davies 2011
|
---|
na
|
3
|
1
|
1
|
1
|
28
|
36
|
17
|
10
|
Sex
|
M
|
1
|
1
| |
1
|
17
|
10
|
8
|
NS
|
F
|
2
| |
1
| |
11
|
26
|
9
|
Age range (years)
|
14.5 – 21
|
19
|
8
|
9
|
3 – 34
|
19 – 60
|
>10
|
NS
|
Genotype
|
TSC1
| | | | |
4
| | | |
TSC2
|
3
|
1
|
1
|
1
|
10
|
14
| | |
Unknown
| | | | |
14
|
22
|
17
|
10
|
Rapamycin
|
Dose (mg/day)
|
2 – 7
|
0.5
|
1
|
5 – 7
|
3b
|
2 – 6
|
1
|
0.5c
|
Trough (ng/ml)
|
7.7 – 10.9
|
4 – 5
|
3.3 – 4.5
|
10 – 15
|
5 – 15
|
3 – 15
|
4 – 8d
|
3 – 6
|
-
NS Not specified
-
aNumber of patients included in the analyses
-
bmg/m2
-
cmg/m2/day
-
dng/dl