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Figure 3 | Orphanet Journal of Rare Diseases

Figure 3

From: Long term follow-up to evaluate the efficacy of miglustat treatment in Italian patients with Niemann-Pick disease type C

Figure 3

Evolution over time of the mean composite severity score (MCSS) during miglustat treatment in different groups of neurologically symptomatic patients, classified for the MCSS at baseline. Patients with a) MCSS ≤ 0.1 (n = 2), b) patients with MCSS between > 0.1 and ≤ 0.3 (n = 3), c) patients with MCSS > 0.3 and ≤ 0.5 (n = 7) and d) patients with MCSS > 0.5 (n = 11).

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Orphanet Journal of Rare Diseases

ISSN: 1750-1172