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Figure 2 | Orphanet Journal of Rare Diseases

Figure 2

From: Long term follow-up to evaluate the efficacy of miglustat treatment in Italian patients with Niemann-Pick disease type C

Figure 2

Evolution over time of the mean composite severity score (MCSS) during miglustat treatment in different groups of patients, classified for the latency between the onset of neurological manifestations and start of therapy (LAG). Patients with a) LAG ≤ 3.5 years (n = 7); b) LAG between >3.5 and ≤ 7 years (n = 7); c) LAG > 7 years (n = 9).

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Orphanet Journal of Rare Diseases

ISSN: 1750-1172