Table 3 Candidates for 51 and 53 exon skipping for restoration of dystrophin expression (source: www.clinicaltrials.gov )
51 exon skipping | 53 exon skipping | ||||
|---|---|---|---|---|---|
Deleted exon(s) | No. of individuals | % of registrants | Deleted exon(s) | No. of individuals | % of registrants |
45-50 | 8 | 3.5% | 52 | 3 | 1.3% |
47-50 | 2 | 0.9% | 47-52 | 1 | 0.4% |
48-50 | 4 | 1.7% | 48-52 | 3 | 1.3% |
49-50 | 2 | 0.9% | 49-52 | 2 | 0.9% |
50 | 2 | 0.9% | 50-52 | 1 | 0.4% |
52 | 3 | 1.3% | |||
52-63 | 0 | 0% | |||
Total | 21 | 9.2% | 10 | 4.3% | |