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Table 3 Candidates for 51 and 53 exon skipping for restoration of dystrophin expression (source: www.clinicaltrials.gov )

From: A comprehensive database of Duchenne and Becker muscular dystrophy patients (0–18 years old) in East China

51 exon skipping 53 exon skipping
Deleted exon(s) No. of individuals % of registrants Deleted exon(s) No. of individuals % of registrants
45-50 8 3.5% 52 3 1.3%
47-50 2 0.9% 47-52 1 0.4%
48-50 4 1.7% 48-52 3 1.3%
49-50 2 0.9% 49-52 2 0.9%
50 2 0.9% 50-52 1 0.4%
52 3 1.3%    
52-63 0 0%    
Total 21 9.2%   10 4.3%