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Table 3 Numbers of recently treated patients given each therapeutic option during ERT shortages according to date

From: The French Gaucher’s disease registry: clinical characteristics, complications and treatment of 562 patients

ERT/SRT

2009/06/01

2009/06/30

2009/08/30

2010/04/01

2010/12/31

Imiglucerase*

     

>15 years

176

153

71

105

98

≤15 years

32

32

25

27

28

Velaglucerase

45

Taliglucerase

24

Miglustat

11

14

20

22

21

Without treatment

28

48

131

93

31

Total

247

247

247

247

247

  1. Note that recent refers to 2009–2010, i.e., the last 2 years.
  2. *Only imiglucerase was prescribed to adults (>15 years) or children (≤15 years).