Patient 8a | Patient 9a | Mean (SD) | |
---|---|---|---|
PedsQL total score at baseline | 48.9 | 57.6 | 53.3 (6.2) |
Change in PedsQL total score at Week 52 | 28.3 | 3.3 | 15.8 (17.7) |
Percent change in total PedsQL score at Week 52 | 57.8 | 5.7 | 31.7 (36.8) P = 0.0311 |
PF | 34.4 | − 9.4 | 12.5 (30.9) |
PH | 25.0 | 10.0 | 17.5 (10.6) |
Body weight, percent change | − 20.1 | − 2.4 | − 11.2 (12.5) |