Fig. 1From: Development and validation of Gaucher disease type 1 (GD1)-specific patient-reported outcome measures (PROMs) for clinical monitoring and for clinical trialsOverview of the development and validation of the ctGD1-PROM. ctGD1-PROM clinical trial (17-item) GD1-specific patient-reported outcome measure questionnaire, GD1/3 Gaucher disease type 1/3, rmGD1-PROM routine monitoring (24-item) GD1-specific patient-reported outcome measure questionnaireBack to article page