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Table 3 PedsQL scores

From: Sebelipase alfa enzyme replacement therapy in Wolman disease: a nationwide cohort with up to ten years of follow-up

 

Patient 1 (%)

Patient 2 (%)

Patient 3 (%)

Patient 4 (%)

Patient 5 (%)

Patient evaluation

71

61

n.a

80

n.a

 Physical functioning (8 items)

75

56

n.a

88

n.a

 Emotional functioning (5 items)

60

60

n.a

90

n.a

 Social functioning (5 items)

70

70

n.a

70

n.a

 School functioning (3 or 5 items)

75

60

n.a

70

n.a

Parental evaluation

82

51

85

85

100

 Physical functioning (8 items)

75

47

84

91

100

 Emotional functioning (5 items)

80

75

70

80

100

 Social functioning (5 items)

85

45

100

100

100

 School functioning (3 or 5 items)

90

40

n.a

65

n.a

  1. n.a. not applicable