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Table 3 PedsQL scores

From: Sebelipase alfa enzyme replacement therapy in Wolman disease: a nationwide cohort with up to ten years of follow-up

  Patient 1 (%) Patient 2 (%) Patient 3 (%) Patient 4 (%) Patient 5 (%)
Patient evaluation 71 61 n.a 80 n.a
 Physical functioning (8 items) 75 56 n.a 88 n.a
 Emotional functioning (5 items) 60 60 n.a 90 n.a
 Social functioning (5 items) 70 70 n.a 70 n.a
 School functioning (3 or 5 items) 75 60 n.a 70 n.a
Parental evaluation 82 51 85 85 100
 Physical functioning (8 items) 75 47 84 91 100
 Emotional functioning (5 items) 80 75 70 80 100
 Social functioning (5 items) 85 45 100 100 100
 School functioning (3 or 5 items) 90 40 n.a 65 n.a
  1. n.a. not applicable