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Table 2 Results in patients with MPS IVA treated with elosulfase alfa

From: Clinical features and health-related quality of life in adult patients with mucopolysaccharidosis IVA: the Spanish experience

Patient number

Time on ERT, years

FVC (mL)

FEV1 (mL)

6MWT (m)

Before ERT

Last visit

Before ERT

Last visit

Before ERT

Last visit

1

1

1663

1610

1361

1358

125

150

2

1

1430

1452

1148

1154

39

86.4

3

6

938

1318

896

1068

32

424

4

4

2460

2690

2180

2360

5

4

780

870

680

730

302

351

  1. 6MWT, six-minute walk test; ERT, enzyme replacement therapy; FEV1, forced expiratory volume in 1 s; FVC, forced vital capacity