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Table 1 Primary outcome results

From: Long-term effectiveness of carglumic acid in patients with propionic acidemia (PA) and methylmalonic acidemia (MMA): a randomized clinical trial

 

Overall

Standard therapy N = 17

Carglumic acid N = 16

Mean total ER visits (STD)

9.64 ± 9.12

12.76 ± 11.18

6.31 ± 4.61

Min

0.00

0.00

0.00

Max

41.00

41.00

16.00

Total ER visits

 0 visits n (%)

5 (15.15)%

3 (17.65%)

2 (12.50%)

 1–2 visits n (%)

3 (9.09)%

1 (5.88%)

2 (12.50%)

 3–4 visits n (%)

4 (12.12)%

2 (11.76%)

2 (12.50%)

 5–6 visits n (%)

4 (12.12)%

1 (5.88%)

3 (18.75%)

 More than 6 Visits n (%)

17 (51.52)%

10 (58.82%)

7 (43.75%)