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Table 6 Mean change in ROM from baseline to 2 years for treated and untreated groups

From: A review of the clinical outcomes in idursulfase-treated and untreated Filipino patients with mucopolysaccharidosis type II: data from the local lysosomal storage disease registry

 

Treated (n = 8)

Untreated (n = 32)

Baseline (mean °)

Year 2 (mean °)

Change* (°)

Baseline (mean °)

Year 2 (mean °)

Change* (°)

Shoulder Flexion

111

101

− 10

90.38

86.5

− 3.88

Shoulder Extension

53.75

61.25

7.5

100

90

− 10

Shoulder Abduction

99.13

98.4

− 0.725

85.63

87.78

2.15

Shoulder Internal Rotation

55

67

12

40

30

− 10

Shoulder External Rotation

52.5

59.25

6.75

35

40

5

Elbow Flexion

93.13

89.5

− 3.63

109.17

104.83

− 4.33

Elbow Extension

111

− 45

66

− 122.5

− 112.5

10

Elbow Supination

10

10

0

80

80

0

Elbow Pronation

35

55

20

80

62.5

− 17.5

Wrist Flexion

46.2

32.5

− 13.7

33.75

6.25

− 27.5

Wrist Extension

22.9

27.5

4.6

25

9.13

− 15.88

Wrist Ulnar Deviation

No information

No information

No information

25

2.5

− 22.5

Wrist Radial Deviation

25

20

− 5

No information

No information

No information

Hip Flexion

126.08

108.83

− 17.25

No information

No information

No information

Hip Extension

8.75

12.25

3.5

No information

No information

No information

Hip Abduction

36.25

46.75

10.5

No information

No information

No information

Hip Internal Rotation

42.5

39.5

− 3

No information

No information

No information

Hip External Rotation

50

50.25

0.25

No information

No information

No information

Knee Flexion

119.13

122.75

3.63

96.28

127.08

30.81

Knee Extension

109.5

− 122.5

− 13

No information

No information

No information

Ankle Dorsiflexion

1.67

4.17

2.5

5

8.13

3.13

Ankle Plantarflexion

37.33

38.38

1.04

40

27.5

− 12.5

Ankle Eversion

5.5

3.75

− 1.75

No information

No information

No information

Ankle Inversion

7.5

14

6.5

No information

No information

No information

  1. *Negative change in ROM: more limited joint mobility; positive change in ROM: improvement in mobility overtime