Skip to main content
Fig. 3 | Orphanet Journal of Rare Diseases

Fig. 3

From: Investigating health-related quality of life in rare diseases: a case study in utility value determination for patients with CLN2 disease (neuronal ceroid lipofuscinosis type 2)

Fig. 3

Mean utility values of patients treated with cerliponase alfa and standard care (mapped to EQ-5D-3L). Summary values were produced from the returned EQ-5D-5L questionnaires and results were mapped to equivalent EQ-5D-3L utility values using the Van Hout algorithm [23]. Mean values ± 1 standard error are shown on the chart. Utility values are given on a scale where 1 is equivalent to perfect health, and 0 equivalent to death. UK value set. VL, vision loss; PC, palliative care

Back to article page

Orphanet Journal of Rare Diseases

ISSN: 1750-1172