Skip to main content
Fig. 1 | Orphanet Journal of Rare Diseases

Fig. 1

From: Investigating health-related quality of life in rare diseases: a case study in utility value determination for patients with CLN2 disease (neuronal ceroid lipofuscinosis type 2)

Fig. 1

Mean utility values across disease stages using the unmapped EQ-5D-5L value set. Mean values ± 1 standard error are shown on the chart. Utility values are given on a scale where 1 is equivalent to perfect health, and 0 equivalent to death. UK value set. Asterisks (*) indicate a statistically significant difference between treatment with standard care and cerliponase alfa using a paired t-test, p < 0.05. VL, vision loss; PC, palliative care

Back to article page

Orphanet Journal of Rare Diseases

ISSN: 1750-1172