From: The multi-domain responder index: a novel analysis tool to capture a broader assessment of clinical benefit in heterogeneous complex rare diseases
Assessment
Pearson correlation with CHAQ/HAQa, N = 76
p value
6MWT
 − 0.24
0.032
FVC
 − 0.19
0.091
Shoulder ROM
 − 0.23
0.051
O’Brien rank score (6MWT, FVC, Shoulder ROM)
 − 0.50
 < 0.001