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Table 5 Frequency of ranking domain in top 5 by current patient age

From: Validation of the 5-domain Niemann-Pick type C Clinical Severity Scale

n (%) 6 months–3 years
(n = 5)
4–17 years
(n = 17)
 ≥ 18 years
(n = 27)
Overall
(n = 49)
Ambulation 4 (80.0) 13 (76.5) 24 (88.9) 41 (83.7)
Fine motor skills 2 (40.0) 4 (23.5) 16 (59.3) 22 (44.9)
Speech 3 (60.0) 11 (64.7) 18 (66.7) 32 (65.3)
Swallow 4 (80.0) 11 (64.7) 20 (74.1) 35 (71.4)
Cognition 2 (40.0) 9 (52.9) 12 (44.4) 23 (46.9)