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Fig. 2 | Orphanet Journal of Rare Diseases

Fig. 2

From: Impact of long-term elosulfase alfa treatment on clinical and patient-reported outcomes in patients with mucopolysaccharidosis type IVA: results from a Managed Access Agreement in England

Fig. 2

Six-minute walk test (6MWT) distance over time compared to results from untreated patients from the MOR-001 natural history study (MOR-001 data linearly extrapolated beyond year 2) (a); box plot of 6MWT at baseline and at last measurement (N = 41; mean follow-up 4.9 years) (b). In the box plot, lines show medians and first and third quartiles; asterisks show means

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Orphanet Journal of Rare Diseases

ISSN: 1750-1172