Skip to main content

Table 5 Ricarte Soto Law – Covered Rare Diseases [37]

From: A civil society view of rare disease public policy in six Latin American countries

 Disease/ConditionTreatment
Current Coverage
 1Mucopolysaccharidosis ILaronidase
 2Mucopolysaccharidosis IIIdursulfase
 3Mucopolysaccharidosis VIGalsulfase
 4TyrosinemiaNitisinone
 5Gaucher DiseaseTaliglucerase or Imiglucerase
 6Fabry DiseaseAgalsidase Alfa or Beta
 7Pulmonary Arterial Hypertension (Group 1)Ambrisentan, Bosentan, or Iloprost
 8Hereditary AngioedemaC1 Esterase Inhibitor
Additions for Coverage beginning July 1, 2019
 9Epidermolysis Bullosa (dystrophic or junctional)Treatment Pack
 10Amyotrophic Lateral Sclerosis (moderate to severe)Technical Assistance and Devices
 11Gastrointenstinal Stromal Tumor (GIST)Imatinib or Sunitinib
 12Psoriatic Arthritis (moderate to severe, refractory)Golimumab, Etanercept, Adalimumab, or Secukinumab
 13Ulcerative Colitis (moderate to severe, refractory)Golimumab or Adalimumab for moderate; Infliximab for severe
 14Myelofibrosis (primary and secondary to other myeloproliferative neoplasms)Ruxolitinib
 15Huntington’s Disease (chorea)Tetrabenazina