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Fig. 3 | Orphanet Journal of Rare Diseases

Fig. 3

From: Treatment preference among patients with spinal muscular atrophy (SMA): a discrete choice experiment

Fig. 3

Conditional logit model estimates for SMA treatment preferences by sub-groups. a Change in motor function: improvement versus stable. b Change in pulmonary function: improvement versus stable. c Drug is approved for: patients < 2 years of age versus pediatric and adult patients. d Route of administration: intravenous infusion versus intrathecal spinal injection. e Route of administration: oral administration versus intrathecal spinal injection. f Potential risk: moderate versus mild. g Potential risk: serious, or life-threatening versus mild

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