From: A charitable access program for patients with lysosomal storage disorders in underserved communities worldwide
Gaucher disease
Fabry disease
Hunter syndrome (MPS II)
N
142
16
41
Sex, n (%)
Male
84 (59.2)
16 (100.0)
41 (100.0)
Female
58 (40.8)
0
Age category, years
0–10
68
27
11–20
34
12
21–30
14
9
2
31–40
4
41–50
10
> 51
7
1