Skip to main content
Fig. 1 | Orphanet Journal of Rare Diseases

Fig. 1

From: Treatment outcomes following continuous miglustat therapy in patients with Niemann-Pick disease Type C: a final report of the NPC Registry

Fig. 1

Patient flow. * Patients who had periods of treatment and nontreatment and had been treated with miglustat for < 90% of the observation time or had one period without miglustat lasting more than 28 days. † Among patients continuously treated with miglustat, 216/241 had received miglustat prior to enrollment for a varying period

Back to article page

Orphanet Journal of Rare Diseases

ISSN: 1750-1172