From: Longitudinal natural history of type I spinal muscular atrophy: a critical review
 | NH DATA | PLACEBO |
---|---|---|
Number of patients(n) | 22 | 41 |
Age at baseline | ||
Mean (days) | 154 | 181 |
Range (days) | 30–210 | 30–262 |
CHOP INTEND scores(mean + SD) | 27.36 + 8,54 | 28.42 + 7.56 |
CHOP INTEND < 20n/tot (%) | 4/22 (18%) | 4/41 (10%) |
CHOP INTEND 20–40n/tot (%) | 16/22 (73%) | 34/41 (83%) |
CHOP INTEND > 40n/tot (%) | 2/22 (9%) | 3/41 (7%) |