From: Expanded access with intravenous hydroxypropyl-β-cyclodextrin to treat children and young adults with Niemann-Pick disease type C1: a case report analysis
Patient ID
Slope pre-IV
Slope post-IV
p-value
SEQ1
7.55
0.96
< 0.001
SEQ2
0.72
SEQ3
2.32
−0.97
SEQ4
3.60
−0.75
0.015
SEQ5
1.00
1.39
0.616
SEQ6
0
0.18
0.236
SEQ7
N/A
4.19
n/a
SEQ8
0.37
SEQ9
1.29
IV1
1