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Table 4 Summary of age inclusion criteria and requirements for neurological signs. The neurological sign requirements are unique to each clinical study

From: Annual severity increment score as a tool for stratifying patients with Niemann-Pick disease type C and for recruitment to clinical trials

Trial Selected Inclusion Criteria References/Clinical Trial Identifier
Age Neurological sign
Miglustat >  12 + [3]
Arimoclomol 2–18 + NCT02612129
2-hydroxypropyl-β-cyclodextrin 2–25 + NCT02534844
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