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Table 1 The demographics of the patients in the two clinical centers are summarized

From: Annual severity increment score as a tool for stratifying patients with Niemann-Pick disease type C and for recruitment to clinical trials

Centre Total Median age (years) by centre at first measurement Female Male Median age (years) at first measurement (female) Median age (years) at first measurement (male) Repeat measure median Range of number of repeat measures Repeat measures in years (median, min, max) Patients on miglustat therapy at any point in the study Patients with seizure recorded on at least one visit
Manchester 13 11.16 8 5 12.77 3.92 5 3–9 4.01, 1.05, 6.36 12 (92%) 5 (38.5%)
Mainz 25 12.45 11 14 11.61 16.76 3 2–7 3.50, 0.94, 5.16 24 (96%) 13 (52.0%)
  1. Age in years at first measurement reflects patient age at the first clinical visit included in this study
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