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Fig. 8 | Orphanet Journal of Rare Diseases

Fig. 8

From: Annual severity increment score as a tool for stratifying patients with Niemann-Pick disease type C and for recruitment to clinical trials

Fig. 8

a Total Clinical Severity Score and b ASIS scores (total severity score/age at time of assessment) of NPC patients post-commencement of treatment with 5 g/day Acetyl-DL-Leucine. The initial severity score (and hence ASIS) of one patient was notably higher than that of the other nine. This patient’s data is therefore provided as a separate graph. Each assessment is represented by one data point

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Orphanet Journal of Rare Diseases

ISSN: 1750-1172