From: Research, diagnosis and education in inborn errors of metabolism in Colombia: 20 years’ experience from a reference center
Tissue
AAV-GALNS
AAV-SUMF1
Bone-tagged
Plasma
8.5
19.4
NA
Liver
21.9
36.6
24.3
Spleen
4.5
5.4
3.2
Kidney
3.1
1.8
Lung
4.2
4.1
3.0
Heart
6.5
30.6
61.8
Brain
4.0
9.1
35.8
Bone marrow
2.0
10.4
13.8
Bone (leg)
0.2
33.3
41.9